I'm kinda stoked that Aurora Therapeutics is working on this gene-editing stuff, tbh 
it could be game-changing for rare disease patients like KJ who didn't have many options before. But, I do worry about the limitations of using base editing and whether it's really enough to tackle all those different mutations in PKU. Plus, I'd love to see more transparency around the data they're using to get FDA approval 
. And, can we talk about how we ensure this tech doesn't end up benefiting only a select few who have access to top-notch medical care? We need to make sure it's available to everyone in need, no matter what their financial situation is 
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it could be game-changing for rare disease patients like KJ who didn't have many options before. But, I do worry about the limitations of using base editing and whether it's really enough to tackle all those different mutations in PKU. Plus, I'd love to see more transparency around the data they're using to get FDA approval . And, can we talk about how we ensure this tech doesn't end up benefiting only a select few who have access to top-notch medical care? We need to make sure it's available to everyone in need, no matter what their financial situation is .
gotta feel good about this new startup, Aurora Therapeutics 
they're using Crispr tech to tackle some super rare diseases that have been kinda stuck with limited treatment options... phenylketonuria (PKU) is one example where they're trying to create personalized therapies that can actually make a difference for patients who are struggling to find effective treatments 
the fact that they're able to use a new FDA pathway that doesn't require hundreds of test subjects is huge, and it's awesome to see a Nobel Prize winner like Jennifer Doudna leading the charge